OMIA:002179-9823 : Stargardt disease 1 in Sus scrofa (pig)

In other species: dog , fat sand rat

Categories: Vision / eye phene

Links to possible relevant human trait(s) and/or gene(s) in OMIM: 248200 (trait) , 601691 (gene)

Links to relevant human diseases in MONDO:

Single-gene trait/disorder: unknown

Disease-related: yes

Species summary: This phene includes references to studies involving gene edited or genetically modified organisms (GMO).

Genetic engineering: Yes - variants have been created artificially, e.g. by genetic engineering or gene editing
Have human generated variants been created, e.g. through genetic engineering and gene editing

Associated gene:

Symbol Description Species Chr Location OMIA gene details page Other Links
ABCA4 ATP binding cassette subfamily A member 4 Sus scrofa 4 NC_010446.5 (123202720..123333044) ABCA4 Ensembl, NCBI gene

Contact us

If you notice anything missing or in need of change, please contact us at: [email protected].

Cite this entry

Nicholas, F. W., Tammen, I., & Sydney Informatics Hub. (2023). OMIA:002179-9823: Online Mendelian Inheritance in Animals (OMIA) [dataset]. https://omia.org/. https://doi.org/10.25910/2AMR-PV70

References

Note: the references are listed in reverse chronological order (from the most recent year to the earliest year), and alphabetically by first author within a year.

2025 Ferla, R., Pugni, E., Lupo, M., Tiberi, P., Fioretto, F., Perota, A., Duchi, R., Lagutina, I., Gesualdo, C., Rossi, S., Ventrella, D., Elmi, A., McClinton, B., Toomes, C., Xu, T., Molday, R.S., Surace, E.M., Simonelli, F., Bacci, M.L., Galli, C., Memon, M.A., Shams, N., Auricchio, A., Trapani, I. :
Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models. Sci Adv 11:eadt9354, 2025. Pubmed reference: 40138422. DOI: 10.1126/sciadv.adt9354.
2024 Wei, S.C., Cantor, A.J., Walleshauser, J., Mepani, R., Melton, K., Bans, A., Khekare, P., Gupta, S., Wang, J., Soares, C., Kiwan, R., Lee, J., McCawley, S., Jani, V., Leong, W.I., Shahi, P.K., Chan, J., Boivin, P., Otoupal, P., Pattnaik, B.R., Gamm, D.M., Saha, K., Gowen, B.G., Haak-Frendscho, M., Janatpour, M.J., Silverman, A.P. :
Evaluation of subretinally delivered Cas9 ribonucleoproteins in murine and porcine animal models highlights key considerations for therapeutic translation of genetic medicines. bioRxiv , 2024. Pubmed reference: 39803585. DOI: 10.1101/2024.12.30.630799.
2023 Wimmer, T., Sawinski, H., Urban, A.M., Motlik, J., Stieger, K. :
Rapid and reliable quantification of prime editing targeting within the porcine ABCA4 gene using a BRET-based sensor. Nucleic Acid Ther 33:226-232, 2023. Pubmed reference: 36857739. DOI: 10.1089/nat.2022.0037.

Edit History


  • Created by Imke Tammen2 on 08 Mar 2023
  • Changed by Imke Tammen2 on 18 Dec 2023